Atp7b位于小鼠的8号染色体,采用CRISPR/Cas技术,设计sgRNA和ssDNA,通过高通量电转受精卵方式,获得Atp7b基因条件性敲除小鼠,性成熟后取精子冻存。
相关疾病:
Wilson Disease
Spastic Ataxia
Wolff Mental Retardation Syndrome
Menkes Disease
Liver Cirrhosis
Ovarian Cancer
Liver Disease
Hemochromatosis, Type 1
Dystonia
Cataract